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  • CMTA-STAR Alliance Partner Vanda Pharmaceuticals Receives FDA Rare Pediatric Disease Designation for CMT2S Therapy Candidate 
    CMTA-STAR Alliance Partner Vanda Pharmaceuticals Receives FDA Rare Pediatric Disease Designation for CMT2S Therapy Candidate

    CMTA Strategy to Accelerate Research (CMTA-STAR) Alliance Partner Vanda Pharmaceuticals has announced that the U.S. Food…

  • More Miles, Less Fatigue: Walking Poles and CMT 
    Walking Poles and CMT

    Travel means more time on your feet, navigating new terrain like cobblestones, stairs, gravel, or uneven pavement.…

  • Is Spinal Fluid the Way to Gene Therapy in CMT? What a Decade of Research Reveals 
    Is Spinal Fluid the Way to Gene Therapy in CMT?

    Most kinds of CMT come from a problem in a single gene. Repairing that faulty…

  • CMTA Leading the Way in CMT1A
    CMTA Leading the Way in CMT1A

    CMTA is leading a coordinated CMT1A research strategy that connects disease models, drug development, biomarkers,…

  • CMTA research takes the stage at PNS
    CMTA research takes the stage at PNS

    PNS 2026 showcased CMTA’s role in advancing CMT research across the translational pipeline, from biomarkers…

  • What Filspari Means for People with CMTDIE 
    What Filspari Means for People with CMTDIE

    FDA approval of Filspari creates a new treatment option for FSGS that may benefit some…

  • CMTA Expands Preclinical Toolbox with New CMT1A Assay
    New CMT1A Assay Now Available

    CMTA expands its Preclinical Toolbox with a new CMT1A assay, providing researchers with a human-relevant…

  • What 465 People with CMT1A Want Researchers to Know
    What 465 People with CMT1A Want Researchers to Know

    Results from a patient survey conducted by CMTA, CMT France, and Nervosave Therapeutics highlight what…

  • The Biggest Battle Wasn’t CMT
    The Biggest Battle Wasn’t CMT

    Arienna Hauser-Brown reflects on growing up with Charcot-Marie-Tooth disease (CMT) and how learning to overcome…

  • Fighting Forward: My Life with CMT
    Fighting Forward: My Life with CMT

    Mother of three shares her biohacking journey with CMT.

  • Occupational Therapy Can Help Your Hands Keep Working 
    Occupational Therapy Can Help Your Hands Keep Working

    Tying your shoes. Opening a jar. Picking up a coin from the counter. Texting. The…

  • When Your Hand Needs a Hand: How Splints Support Function and Comfort 
    When Your Hand Needs a Hand: How Splints Support Function and Comfort

    CMT affects hands and wrists in different ways and at different points in life. Some people notice…