2024 CMTA Patient & Research Summit Registration is Now Open Advancements in CMT1A and CMT1B Research Highlight CMTA’s Impact Advancing the Understanding of CMT2A and CMT2F: A Call to Beat CMT Alliance Partner NMD Pharma A/S Launches Phase II SYNAPSE-CMT Trial with First Patient Dosed at CMTA Center of Excellence Breakthrough in CMT1A Research: Community Efforts Drive Success of Dental Stem Cell Model Bruce R Conklin, MD Joins the CMTA STAR Advisory Board Chris Oviatt – Golfer with CMT CMT-SORD: Bringing the Science Down to Earth | Shooting Star Ep. 3 CMT2F Natural History Study Nears Full Recruitment as Biomarker Analysis Begins CMT2S Breakthrough CMTA Alliance Partner Applied Therapeutics Plans to Submit an NDA for CMT-SORD, a Potential First Approval for the Treatment of any type of CMT CMTA Alliance Partner, Applied Therapeutics, Announces Positive 12-Month Results in its Ongoing INSPIRE Phase III Trial for CMT-SORD CMTA and INC Forge Groundbreaking Alliance to Accelerate Comprehensive Research Across All Charcot-Marie-Tooth Disease Types CMTA Announces New Center of Excellence at Duke University Hospital CMTA Announces New Center of Excellence at Virginia Commonwealth University CMTA Announces New Center of Excellence in Kentucky CMTA Announces New Center of Excellence in Thailand CMTA Announces New Center of Excellence in the United Kingdom CMTA Appoints David Skarinsky to its Therapy Expert Board CMTA Appoints Katherine Forsey Chief Research Officer CMTA Appoints Science and Technology Veteran, Patricia Verduin, PhD, to the Board of Directors CMTA Invests $423K to Accelerate CMT Diagnostics and Gene Discovery CMTA Partners with Actio Bio on CMT2C Focus Group CMTA Supports the Accelerating Kids’ Access to Care Act (H.R.4758 / S.2372) CMTA-INC Strategic Alliance Announces the 2025 Inherited Neuropathy Fellowship CMTA-STAR Alliance Partner Actio Biosciences Receives FDA Orphan Drug Designation and Rare Pediatric Disease Designation for Their Treatment in Development for CMT2C CMTA-STAR Alliance Partner NMD Pharma Announces FDA Orphan Drug Designation for NMD670 CMTA-STAR Alliance Partner NMD Pharma Publishes Transformative Study on Charcot-Marie-Tooth Disease CMTA-STAR Clinical Expert Board Co-Chair Prof. Mary Reilly Honored with Prestigious MBE CMTA-STAR Collaboration Celebrates a Decade of CMT Genetic Discovery Through the GENESIS Database CMTA’s $240K Investment Targets Gene Replacement Therapy in CMT4 Subtypes CMTA’s New Video Aims to Increase Awareness About CMT CMTA’s Strategic Investment Advances Research for CMT1A and CMT1B CMTA’s CRISPR Research Initiative Advances for CMT1A and CMT1B Diana Bharucha-Goebel, MD Joins the CMTA-STAR Advisory Board DNA-Based Therapeutics: A Promising Future for CMT2E Treatment Encouraging News in CMT Research from CMTA-STAR Alliance Partner Alesta Therapeutics Exploring New Therapeutic Pathways for CMT1B: UPR Activation From Gene Discovery to Gene Editing: Closing the Diagnostic Gap and Developing CRISPR/Cas9 Capabilities in CMT Gene Replacement Therapy in CMT4 Subtypes Gene Therapy for CMT1A, 1B, and X1: Progress in Nanoparticles Leading the Way: The CMTA Invests More Than $200K in Cutting-Edge CMT1A Organoid Research Learn How CMTA is Accelerating Research and Empowering Patients Mindset Strategies for Kids and Teens with CMT Nanoparticles for CMT1A, CMT1B, and CMTX1: A New Frontier in Gene Therapy New Law Makes Flying Easier for People Living With Charcot-Marie-Tooth Disease NMD Pharma Receives FDA Approval to Initiate Phase II Clinical Trial of NMD670 in CMT Patients Progress Update: Timmerman’s CMT1A Organoid Project Shows Early Success Recap: 2024 CMTA Patient & Research Summit Repurposing Drugs for CMT1A: An Encouraging Approach Simply CMT Podcast Episode 2: Jonah Berger TAKE ACTION! Sign the Petition to Accelerate CMT-SORD The Charcot-Marie-Tooth Association Launches Gadget Store The CMTA Appoints Professor Charlotte Sumner, M.D., to its Scientific Advisory Board The CMTA Mourns the Loss of Scientific Advisory Board Member and Esteemed CMT Clinical Researcher Vera Fridman, MD joins the CMTA STAR Advisory Board Swag Up for CMT Awareness Month! Employment Opportunities at the CMTA Pete Foley Joins CMTA Board of Directors The Summer 2021 CMTA Report The Spring 2021 CMTA Report – Special Research Edition CMTA-STAR Awards $1.1 Million for CMT1X, CMT2A Clinical Trials Faces of CMT Photography Competition The Winter 2020-2021 CMTA Report Who Inspires You to Give? The Fall 2020 CMTA Report CMTA and Pharnext Enter Biomarker Research Collaboration CMT Awareness Month 2020: Be a Champion Type 2 Update: One Patient’s Diagnostic Odyssey with SORD The 2020 Summer CMTA Report Breakthrough Guide to Orthopedic Surgery for CMT CMTA Camp Footprint Has Gone Virtual for 2020 CMTA 2019 Annual Report Highlight Reel Craig Zeltsar Joins CMTA Board of Directors New, Potentially Treatable, Type of CMT Discovered CMT2E Gene Therapy Project Approved The 2020 Spring CMTA Report CMTA Board Approves CMT1B Project Coronavirus (COVID-19) and CMT CMTA Event Schedule Update from CEO Amy Gray Acceleron Announces Topline Results from the Phase 2 Trial of ACE-083 in Patients with Charcot-Marie-Tooth Disease Coronavirus (COVID-19) Update CMTA Funds Cutting-Edge Gene Editing Studies for Type 2 CMT The 2020 Winter CMTA Report David Coldiron Joins CMTA Board of Directors A Message from Patients to Patients Another $500,000 Pledge to Type 2 Research! The 2019 Fall CMTA Report New Gene Therapy, Type 1/Type 4 Research Projects Approved New Gene Therapy Development Program for CMT2A $1 Million Gift Pledged to CMT Type 2 Research! 2019 Summer CMTA Report Remembering Camp Footprint Finding Friendship at Camp Footprint! Support Our Campers – Whatever It Takes! Camp Help Falling in Love 2019 Spring CMTA Report CMTA Unveils Updated Logo Type 1 CMT Gene Therapy Project Now Underway A Cure for Caroline and Other CMT Stories CMTA-Funded Research Database Identifies New Mutations Three Major Patient Advocacy Groups Focused on CMT Research Collaborating on FDA “Voice of the Patient” Report Regenacy Pharmaceuticals Announces Collaboration with the CMTA to Advance Ricolinostat for the Treatment of Hereditary Neuropathy Volunteer Spotlight: Amy Keller How Balance Walking Can Help Fitness and Living with CMT The CMTA Announces the Funding of a New Research Study for CMT2A CMTA Announces Strategic Partnership with Acceleron to Advance CMT Treatment Options New Mobile App Simplifies Sign-Up for Patient Registry 101 Practical Tips for Dealing with CMT New CEO Takes Helm of the CMTA CMTA-Funded Study on 3-D Printing Technique for Comparing CMT Heel Surgeries Named Game Changer at AAOS Meeting Important Alert: Neurotoxic Medication List Update CMTeen Dolphin Outing in PEOPLE Online MDA and CMTA Fund Grant to Study Gene Therapy in Charcot-Marie-Tooth Disease Invitae Announces Major Expansion of Its Neurology Test Offerings MDA and CMTA Partner to Advance Treatments and Care for Charcot-Marie-Tooth Disease NYSCF and CMTA Announce Largest-Ever Research Resource for Neuropathy Disorders STAR Launches Research for CMT4C Gilles Bouchard Takes Helm of CMTA Board CMT is on TV! PSA on Charcot-Marie-Tooth Disease The New York Stem Cell Foundation and the CMTA Enter Collaboration to Advance Neuropathies Research Your legacy can help bring an end to CMT. Learn how a planned gift can make an impact for generations to come. Now available as a Kindle eBook for only $7.95 Order it today!