MDA and CMTA Fund Grant to Study Gene Therapy in Charcot-Marie-Tooth Disease
…million. MDA and the CMTA are co-funding the grant under a partnership formed in 2016 that aims to advance CMT research, therapy development and clinical care, and increase understanding about…
CMT4 Research
…to advance research for CMT. Support CMT Research View the projects currently active or recently completed in the CMT4 drug development pipeline. CMT4 RESEARCH PROJECTS CMT4A Research CMT Type 4A…
Syracuse Walk4CMT
09/09/2023 @ 9:30 am – 12:00 pm – The Syracuse CMTA branch will be hosting two events this September! The Syracuse CMTA branch will be recognized at the Syracuse Mets baseball game on September 6th at 1:05pm. We will have information about CMT, swag, and will be throwing out the first pitch. A portion of the ticket proceeds will go directly to the […]
2021 CMTA Annual Report
…CMT2A, CMT2D, CMT2E, CMT2F, CMT2K, CMT4A and CMT4C, utilizing several different technologies, including AAV delivery, gene silencing, gene replacement, genome editing using CRISPR-Cas9 and antisense oligonucleotides (ASOs). 6 Biomarkers Clinical…
CMTA Announces New Center of Excellence in the United Kingdom
…London. Staffed by world-renowned expert CMT physicians, clinicians, and researchers, each CMTA Center of Excellence is a patient-focused, multidisciplinary CMT clinic where children, adults, and families affected by CMT receive…
Regenacy Pharmaceuticals Announces Collaboration with the CMTA to Advance Ricolinostat for the Treatment of Hereditary Neuropathy
…About Charcot-Marie-Tooth Association (CMTA) The Charcot-Marie-Tooth Association is a leading patient led nonprofit organization dedicated to finding a cure for CMT. The CMTA’s Strategy to Accelerate Research (STAR) program brings…
Diagnosticando CMT
Diagnosticando CMT Charcot–Marie–Tooth, o CMT, es la neuropatía periférica hereditaria más común y se encuentra en todo el mundo entre todas las razas y grupos étnicos. Descubierto en 1886 por…
Teaching Kids About CMT
…it some thought, I decided to present CMT to the entire class in a very upbeat, interactive, and educational way. My goal was to have the students actually acquire some…
2017_Winter_CMTA_Report
…Regional Branch Manager, michelle@cmtausa.org Kim Magee Director of Finance, kim@cmtausa.org Bethany Meloche Director of Social Media, bethany@cmtausa.org Susan Ruediger Director of Development, sruediger@cmtausa.org Marcia Semmes Director of Print Communications, marcia@cmtausa.org…
CMTA_2020_Annual_Report
…types of CMT, including CMT1A, CMT1X, CMT2A, CMT2D, CMT2E, CMT2F, CMT2K, CMT4A and CMT4C, utilizing a number of different technologies, including AAV delivery, gene silencing, gene replacement, genome editing using…