Shift Pharmaceuticals, CMTA Partner on ASO Treatment for CMT1A
Shift Pharmaceuticals, CMTA Partner on ASO Treatment for CMT1A GLENOLDEN, PENNSYLVANIA, USA, NOVEMBER 3, 2022 — Shift Pharmaceuticals, a privately held company that is developing antisense oligonucleotides (ASOs) to treat…
2021 990 PUBLIC
…Part IV If “Yes,” complete Schedule M If “Yes,” complete Schedule M If “Yes,” complete Schedule N, Part I If “Yes,” complete Schedule N, Part II If “Yes,” complete Schedule…
CMTA Seed Money Draws NIH Support For Type 2 Gene Editing
…of common human genetic variation that can be targeted to excise protein coding or critical regulatory regions and inactivate the disease allele in the majority of patients, regardless of their…
CMTA-STAR Awards Researcher $98,985 For CMT1A Project
…long, or peripheral, nerves to the hands and feet. As the nerves die, the muscles around them follow suit. CMT1A, the most common type of CMT, is caused by a…
CMTA and Applied Therapeutics Announce Collaboration for CMT-SORD
…get free SORD testing by having a nurse come to their home or through their doctor’s office, and the patient perspective will be shared to help shape trials to come….
All Other Types
OTHER TYPES OF CMT: STRATEGY Although there are more than 100 different genes that cause CMT, there are some common symptoms that affect people living with CMT such as axon…
Unidentified Type 2 CMT Research
…role in developing the infrastructure necessary to evaluate CMT therapies. View the projects currently active or recently completed in the Unidentified Type 2 drug development pipeline. UNIDENTIFIED CMT TYPE RESEARCH…
CMTA Preclinical Testing Network
…and pharmaceutical companies working on Charcot-Marie-Tooth neuropathy disorders. To achieve this objective, the CMTA set out to assemble “toolboxes” for different CMT disorders that allow fast and cost-effective pre-clinical evaluation…
CMTA-Funded Research Database Identifies New Mutations
…CMTA supports the development of therapies for the CMT community,” she added, explaining, “As we discover more of the genetic causes of the unidentified forms of CMT, we can strategically…
INC Research Study 6602: Genetics of Charcot Marie Tooth Disease
…Amy Gray said. “Funding this project is another way the CMTA supports the development of therapies for the CMT community,” she added, explaining, “As we discover more of the genetic…