Your legacy can help bring an end to CMT. Learn how a planned gift can make an impact for generations to come.
Breakthrough in CMT1A Research: Community Efforts Drive Success of Dental Stem Cell Model
…for future drug screening and treatment development beyond CMT1A, including CMT1E, HNPP, CMTX1 (aka CMT1X, CMTX), CMT2A, CMT2C, CMT2T, and CMT4A—the additional subtypes from which donations were received. Register With…
Recap: 2024 CMTA Patient & Research Summit
…in potential CMT treatments and ongoing projects aimed at finding a cure. Help for Today Attendees of the 2024 CMTA Patient & Research Summit The Summit provided attendees with many…
Therapeutic Inactivation of CMT2 Disease Alleles with CRISPR
New technologies in gene editing such as CRISPR/Cas9 present a promising opportunity for the treatment of genetic diseases like CMT at the root cause – often just a single base…
Exploring New Therapeutic Pathways for CMT1B: UPR Activation
…developing a potential treatment for CMT1B. This groundbreaking work, led by Maurizio D’Antonio, PhD, focuses on activating the Unfolded Protein Response (UPR), targeting the fundamental issue caused by mutations in…
Central Tennessee CMTA Branch Meeting (Virtual)
08/26/2024 @ 6:00 pm – 7:00 pm – Please join us (via Zoom) for the next meeting of the Central Tennessee CMTA Branch on Monday, August 26th at 6 pm Central Time when we will gather virtually to discuss what to do after receiving a diagnosis of CMT. The session will cover the essential information on available resources, treatment options, and practical strategies […]
Nanoparticles for CMT1A, CMT1B, and CMTX1: A New Frontier in Gene Therapy
…cells while remaining capable of delivering the necessary gene therapies effectively. This delicate balance is crucial for the success of the treatment, as the nanoparticles must be able to traverse…
Repurposing Drugs for CMT1A: An Encouraging Approach
…nerve cells will alleviate CMT symptoms and slow disease progression. This innovative approach to CMT1A treatment involves repurposing an existing FDA-approved drug, which could expedite the availability of a new…
Summer 2024 CMTA Report: A Season of Renewal and Progress
…intelligence revolutionizes CMT diagnosis, treatment, and management with a dedicated feature by CMTA Chief Research Officer Katherine Forsey, PhD, on page 20 in her column, Under the Microscope. Additionally, community…
CMT-SORD: Share Your Story
…help accelerate advancements towards treatments and, ultimately, a cure for this disease. The main goal of this CMT research project is to understand better how CMT-SORD affects the person in…
CMTA Announces New Center of Excellence in Thailand
The Charcot-Marie-Tooth Association (CMTA), the world’s largest philanthropic funder of research aimed at bringing treatments to patients and improving the lives of those living with Charcot-Marie-Tooth disease (CMT), is excited…