All Other Types

…CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be of therapeutic benefit across a variety of CMT types. PROJECT GOAL:…

Fall_2020_CMTA_Report

…an FDA approved drug and similar compounds—could lead to an accelerated treatment for patients. CMT1A Project: The board awarded Dr. Luigi Puglielli, University of Wisconsin Madison, $89,889 to explore a…

Glenn Pfeffer_Tendon Transfer Article_2020

…Tendon Transfers for Treatment of Foot Drop in Charcot-Marie-Tooth Disease: A Biomechanical Evaluation Glenn B. Pfeffer, MD1*, Max Michalski, MD1* , Trevor Nelson, BS1, Tonya W. An, MD, MA1 ,…

2017_Summer_CMTA_Report

…on the brink of some major research breakthroughs that could potentially lead to a treatment for CMT. As I have begun reaching out to our longtime members and supporters, the…

CMTAreportspring24FINALwebSPREADS

…new treatments for CMT, to improve the quality of life for people with CMT, and, ultimately, to find a cure. Registering today as a CMTA patient partner puts you at…

CMTA _2015_Annual_Report

…CMTA is aggressively fighting to find a pharmaceutical treatment, and, ultimately, a cure for all types of CMT. We currently have protocols for developing treatments for the types of CMT…

2021_Winter_CMTA_Report

…the vaccine have on possible future gene therapy treatments or medications? The Food and Drug Admini – stration’s authorization of the Pfizer/BioNTech vaccine did not mention any contraindications for genetic…

2020_CMTA_PFC_Axonal_Update_transcript

…CMT it’s even riskier for companies to work because there hasn’t been a successful clinical trial. There is no treatment. So the risk is viewed as being really high as…

2020_CMTA_PFC_Demyelinating_Update_transcript

…risky business. And in CMT it’s even riskier for companies to work because there hasn’t been a successful clinical trial. There is no treatment. So the risk is viewed as…

The_2018_CMTA_Report_35th_Anniversary_Edition

…or treatment-focused research through STAR in recent years, but the need remains to raise at least $10 million more to support our strategy to deliver treatments to our community. It’s…