The Fall 2021 CMTA Report
…out walking, riding and swimming to raise money for CMTA-STAR research—everything from the Bucks County annual picnic to the daylong extravaganzas mounted by the Vermont Cycle (and Walk!) 4 CMT…
CMTA_2016_Annual_Report
Community Members Taking Action Charcot-Marie-Tooth Association In 2008, the CMTA’s Board of Directors launched its Strategy to Accelerate Research, or STAR, with the aim of translating scientific research into therapies…
What is CMT?
…Research (STAR) in 2008, CMTA has been working with preeminent researchers, clinicians, patients and institutions in the global inherited neuropathy community to capitalize on breakthroughs in genetics. Unlike other neuromuscular…
Novartis Secures $1.3B Deal for CMT Treatment CKD-510
…portfolio. The significance of this collaboration is underscored by the substantial financial investment and the broader landscape of CMT research. HDAC6 has long been a focal point of CMT research,…
New Mobile App Simplifies Sign-Up for Patient Registry
A new mobile app developed by the Rare Diseases Clinical Research Network (RDCRN) makes it easier than ever for CMT patients to sign up for and navigate the network’s patient…
Types of CMT
…because, by nerve conduction characteristics, it is neither demyelinating nor axonal – it is somewhere in between – it is intermediate. Learn more about how CMTA is accelerating research for…
Initiation of Registrational Phase 2/3 Study of AT-007 in SORD Deficiency
…the CMTA’s research efforts are consolidated under the banner of STAR—which brings together the world’s largest network of biotech research partners, research scientists, clinicians and patients—and funds more CMT grants…
CMTA Spring 2024 Report: Progress and Impact that Empowers Communities
…webinars, local meetings, and a Patient and Research Summit. Sue expresses gratitude to the community for their courage, resilience, and commitment. The CMTA’s community-led outreach efforts in 2023 included successful…
Volunteer Spotlight: Amy Keller
…covered with the CMTA STARS Amy has sold to raise funds for CMT research. One fateful day, Amy recalls, she decided she was tired of feeling down about her diagnosis…
How to Contact Your Hometown Media
…their work. The CMTA launched the Strategy to Accelerate Research, or CMTA-STAR, in 2008 to capitalize on breakthroughs in genetics and dramatically speed up the pace of CMT research. Since…