CMTA-STAR Awards Researcher $98,985 For CMT1A Project
…and CMT 1X (GJB1). It is estimated that CMT affects 3+ million people worldwide, regardless of gender, race, or ethnicity. More information can be found at https://www.cmtausa.org/understanding-cmt/what-is-cmt About the CMTA…
Children/School
…prove challenging. How can I enroll my children in testing/studies? Please visit a CMTA Center of Excellence at https://www.cmtausa.org/living-with-cmt/find-help/cmta-centers-of-excellence or enroll your child with the Inherited Neuropathies Consortium at https://www.rarediseasesnetwork.org/cms/inc/….
CMTA Funds Preclinical Work on Modulating Unfolded Protein Response in CMT1B Mice
…companies and patients to expedite the development of treatments for CMT. Since 2008, the CMTA has invested more than $18.5 million in STAR, with plans to invest another $10 million…
Shift Pharmaceuticals, CMTA Partner on ASO Treatment for CMT1A
…“We are thrilled to enter into this collaboration with Shift Pharmaceuticals to broaden the work taking place to develop treatments for the CMT community.” About Shift Pharmaceuticals Shift Pharmaceuticals was…
CMTA Seed Money Draws NIH Support For Type 2 Gene Editing
…is estimated that CMT affects 3+ million people worldwide, regardless of gender, race, or ethnicity. More information can be found at https://www.cmtausa.org/understanding-cmt/what-is-cmt About the CMTA The CMTA is the largest…
CMTA-STAR Awards $354,826 for CMT Clinical Trial
…3+ million people worldwide, regardless of gender, race, or ethnicity. More information can be found at https://www.cmtausa.org/understanding-cmt/what-is-cmt About the CMTA The CMTA is the largest philanthropic funder of CMT research…
CMTA and Applied Therapeutics Announce Collaboration for CMT-SORD
…through its nationwide branch system through North America and more. More information can be found at www.cmtausa.org. About Applied Therapeutics Applied Therapeutics is a clinical-stage biopharmaceutical company developing a pipeline…
All Other Types
…in person at one of the INC’s sites. To learn how to enroll in Project #6601, please visit www.rarediseasesnetwork.org/cms/inc/6601. Once you’ve participated in Project #6601, you may proceed with Project…
Unidentified Type 2 CMT Research
…in person at one of the INC’s sites. To learn how to enroll in Project #6601, please visit www.rarediseasesnetwork.org/cms/inc/6601. Once you’ve participated in Project #6601, you may proceed with Project…
CMTA Preclinical Testing Network
…Therapy Expert Advisory Board, and Clinical Advisory Board. See the full list of advisors at: www.cmtausa.org/research/star-advisory-board/. Single point of contact for agreements. Expert services for study planning and project execution…