STAR insert 2023
…discoveries. CRITICAL RESEARCH RESOURCES AND LEARNINGS • New rodent models of CMT have emerged as crucial testing resources for potential therapies covering CMT1A, CMT2A, CMT1X, CMT2E and CMT1B. The CMTA…
We Are Family
…Do it for our family. On behalf of the entire CMTA family, you have our sincere gratitude. Amy Gray, CMTA Chief Executive Officer, and Jeana Sweeney, CMTA Director of Development…
Acceleron Announces Topline Results from the Phase 2 Trial of ACE-083 in Patients with Charcot-Marie-Tooth Disease
…to the discovery, development, and commercialization of TGF-beta superfamily therapeutics to treat serious and rare diseases, today announced that treatment with ACE-083 in patients with Charcot-Marie-Tooth disease (CMT) did not…
GeneDx Genetic Testing & Whole Exome Sequencing
…diagnoses in patients with CMT. Therefore, GeneDx offers a Core CMT panel, which targets these four most common genes. In addition, GeneDx offers other multigene panels based on a patient’s…
Seattle Focus Group with Acceleron Pharma
We are pleased to announce another opportunity to get involved with the CMTA’s Patients as Partners in Research initiative! The goal of Patients as Partners in Research is to advance…
GeneDx
…diagnoses in patients with CMT. Therefore, GeneDx offers a Core CMT panel, which targets these four most common genes. In addition, GeneDx offers other multigene panels based on a patient’s…
A Comprehensive Guide to Clinical Trials
…approval of new treatments for CMT. Stages of a Clinical Trial Preclinical Testing: Preclinical testing involves studies using human or animal cells and CMT animal models to evaluate the safety…
Corporate Sponsors
…SitnStand CMT community members receive a $50 discount and SitnStand will donate $50 for every purchase to CMTA. Use coupon code “CMTA FRIENDS” to receive the discount. Turbomed Orthotics …
Cynthia Lawrence, Disney Princess and Athlete
…she tries to sew, knit and paint. She is a member of the South Florida CMTA Branch and moderator of the CMTAthletes Facebook group (www.facebook.com/groups/cmtathletes/). And she loves college football….
Getting Started
Register Your Event Contact your CMTA National Events Manager, Andi Cosby (andi@cmtausa.org), with the following information to have your event added to our website. Event Name – this must include…