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CMTA Alliance Partner, NMD Pharma, Announces Encouraging Data with Implications for CMT
…of patients who had CMT1 or CMT2—demyelinating or axonal, respectively, that neuromuscular junction (NMJ) transmission deficits affect some who have CMT and that these deficits correlate with disease severity. Building…
General Questions
…plasma donation should have any effects on CMT or vice versa. Can CMT cause noises in the ears? The auditory nerves can be affected in many forms of CMT. Most…
CMTA-Funded Research Database Identifies New Mutations
…evaluate CMT therapies. “The work in Züchner’s lab aligns perfectly with the CMTA’s Strategy to Accelerate Research (STAR),” CMTA CEO Amy Gray said. “Funding this project is another way the…
MDA and CMTA Fund Grant to Study Gene Therapy in Charcot-Marie-Tooth Disease
…million. MDA and the CMTA are co-funding the grant under a partnership formed in 2016 that aims to advance CMT research, therapy development and clinical care, and increase understanding about…
CMT4 Research
…to advance research for CMT. Support CMT Research View the projects currently active or recently completed in the CMT4 drug development pipeline. CMT4 RESEARCH PROJECTS CMT4A Research CMT Type 4A…
2021 CMTA Annual Report
…CMT2A, CMT2D, CMT2E, CMT2F, CMT2K, CMT4A and CMT4C, utilizing several different technologies, including AAV delivery, gene silencing, gene replacement, genome editing using CRISPR-Cas9 and antisense oligonucleotides (ASOs). 6 Biomarkers Clinical…
Syracuse Walk4CMT
09/09/2023 @ 9:30 am – 12:00 pm – The Syracuse CMTA branch will be hosting two events this September! The Syracuse CMTA branch will be recognized at the Syracuse Mets baseball game on September 6th at 1:05pm. We will have information about CMT, swag, and will be throwing out the first pitch. A portion of the ticket proceeds will go directly to the […]
Nanoparticles for CMT1A, CMT1B, and CMTX1: A New Frontier in Gene Therapy
…Genetics are pioneering the use of nanoparticles to develop gene therapy approaches for three common types of CMT: CMT1A, CMT1B, and CMTX1 (also known as CMT1X or CMTX). The gene…
Regenacy Pharmaceuticals Announces Collaboration with the CMTA to Advance Ricolinostat for the Treatment of Hereditary Neuropathy
…About Charcot-Marie-Tooth Association (CMTA) The Charcot-Marie-Tooth Association is a leading patient led nonprofit organization dedicated to finding a cure for CMT. The CMTA’s Strategy to Accelerate Research (STAR) program brings…
Teaching Kids About CMT
…it some thought, I decided to present CMT to the entire class in a very upbeat, interactive, and educational way. My goal was to have the students actually acquire some…