CMTA and Pharnext Enter Biomarker Research Collaboration
…About CMTA The CMTA is aggressively leading the fight to fund the development of treatments and, ultimately, a cure for CMT. Through its Strategy to Accelerate Research (STAR), the CMTA…
CMT-SORD: Bringing the Science Down to Earth | Shooting Star Ep. 3
…and enthusiasm with important updates on CMTA programs, research, and community impact. In this episode, we dive into CMT-SORD, a unique form of Charcot-Marie-Tooth disease (CMT) linked to mutations in…
CMTA_PT_OT_Guide_9_2018_DT
Nervosave: Shaping the Future of Genetic Therapy for CMT1A
…is looking for: Individuals with genetically confirmed CMT1A Symptomatic individuals with a confirmed family history of CMT1A Parents of children with genetically confirmed CMT1A What’s Involved? Participation involves completing a…
CMTA_PT_OT_Guide_9_2018_DT
CMTA Unveils Updated Logo
…20 pharmaceutical and biotechnology partners, the world’s top CMT scientists collaborating through STAR, and a community powering our efforts, the CMTA is leading the way to a world without CMT….
CMTA and ToolGen Announce CMT1A Collaboration
CMTA and ToolGen Announce Collaboration to Develop Potential Treatment for CMT1A Using Gene Therapy (Glenolden, PA, October 7, 2021) The Charcot–Marie–Tooth Association (CMTA), the largest philanthropic funder of CMT research…
All Other Types
OTHER TYPES OF CMT: STRATEGY Although there are more than 100 different genes that cause CMT, there are some common symptoms that affect people living with CMT such as axon…
CMTA-STAR Alliance Partner Actio Biosciences Receives FDA Orphan Drug Designation and Rare Pediatric Disease Designation for Their Treatment in Development for CMT2C
…designation (RPDD) designation from the FDA for ABS-0871, a TRPV4 inhibitor for treating CMT2C. This achievement represents a crucial step forward for CMT2C patients and the CMT community. “We are…
Alan Jackson shares his CMT story with the Today Show
…Jackson for using his platform to bring awareness to CMT, a neurological disease that affects more than 3 million people worldwide. This CMT Awareness Month, we have seen the CMT…