Type 1 CMT Gene Therapy Project Now Underway

…their behalf. To learn more about the CMTA, please visit www.cmtausa.org. Media contacts: Mary Fiance Director, Public Relations and Communications, MDA (646) 992-2908 mfiance@mdausa.org Marcia Semmes Media Relations, CMTA marcia@cmtausa.org…

Gene Replacement Therapy in CMT4 Subtypes

…using a model replicating CMT4A. If successful, this approach could serve as a template for treating other types of CMT, such as CMT4B1 and CMT4D. “Recent advances in developing desirable…

Type 1 CMT Gene Therapy Project Now Underway

…their behalf. To learn more about the CMTA, please visit www.cmtausa.org. Media contacts: Mary Fiance Director, Public Relations and Communications, MDA (646) 992-2908 mfiance@mdausa.org Marcia Semmes Media Relations, CMTA marcia@cmtausa.org…

2019_Summer_CMTA_Report

…laurel@cmtausa.org Jeana Sweeney Director of Development, jeana@cmtausa.org INSIDE THIS ISSUE RESEARCH CMT4C—Gene Therapy …………………………………………………………………………6 Wearable Biomarkers …………………………………………………………………………..6 CMT COMMUNITY The Doctors of the CMTA ……………………………………………………………………….8 Why We Give…………………………………………………………………………………..14 FUN AND…

2019_Summer_CMTA_Report

…laurel@cmtausa.org Jeana Sweeney Director of Development, jeana@cmtausa.org INSIDE THIS ISSUE RESEARCH CMT4C—Gene Therapy …………………………………………………………………………6 Wearable Biomarkers …………………………………………………………………………..6 CMT COMMUNITY The Doctors of the CMTA ……………………………………………………………………….8 Why We Give…………………………………………………………………………………..14 FUN AND…

CMT1X Research

…therapy for not only CMT1X but also other demyelinating forms of CMT (CMT1A and CMT4C). The CMTA convened a workshop with some of the world’s top gene therapy experts to…

CMT Subtype Biomarkers and Outcome Measures

…this study includes: 2 questionnaires (the CMT Health Index and Patient Global Impression of Change (PGIC)) that explore how you think CMT affects you CMT Functional Outcome Measure (CMT-FOM) which…

The_2018_CMTA_Report_35th_Anniversary_Edition

…Co-Chair, Clinical Expert Board FLASHBACK 1987 The Second International Conference at Columbia University was groundbreaking for the CMTA and the CMT community. mailto:andi@cmtausa.org mailto:frank@cmtausa.org mailto:leslie@cmtausa.org mailto:kim@cmtausa.org mailto:laurel@cmtausa.org mailto:jeana@cmtausa.org https://www.cmtausa.org mailto:info@cmtausa.org…

The_2018_CMTA_Report_35th_Anniversary_Edition

…Co-Chair, Clinical Expert Board FLASHBACK 1987 The Second International Conference at Columbia University was groundbreaking for the CMTA and the CMT community. mailto:andi@cmtausa.org mailto:frank@cmtausa.org mailto:leslie@cmtausa.org mailto:kim@cmtausa.org mailto:laurel@cmtausa.org mailto:jeana@cmtausa.org https://www.cmtausa.org mailto:info@cmtausa.org…

The_2018_CMTA_Report_35th_Anniversary_Edition

…Co-Chair, Clinical Expert Board FLASHBACK 1987 The Second International Conference at Columbia University was groundbreaking for the CMTA and the CMT community. mailto:andi@cmtausa.org mailto:frank@cmtausa.org mailto:leslie@cmtausa.org mailto:kim@cmtausa.org mailto:laurel@cmtausa.org mailto:jeana@cmtausa.org https://www.cmtausa.org mailto:info@cmtausa.org…