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Gene Replacement Therapy in CMT4 Subtypes
…of accelerating gene replacement therapies for CMT, underscoring our leadership in this critical area of research,” said Katherine Forsey, PhD, CMTA Chief Research Officer. “This investment in gene replacement therapy…
CMTA Report_Winter 2024 – STAR Special Edition_Download
2023 CMTA Annual Report
CMTA 2023 Annual Report
Bruce R Conklin, MD Joins the CMTA STAR Advisory Board
…Advisory Board (SAB). The SAB is comprised of world-leading experts who provide scientific input and evaluation of ongoing or proposed CMTA funded research projects and guide the CMTA’s research strategy….
CMT1A Research Breakthrough!
…hopeful breakthrough for medical researchers, healthcare professionals, patients, and families. Ionis researchers used their expertise as a world leader in developing antisense oligonucleotides, which precisely target the products of genes…
Three Major Patient Advocacy Groups Focused on CMT Research Collaborating on FDA “Voice of the Patient” Report
…condition. We thank the HNF for coordinating this important meeting and the MDA for their partnership. We believe this collaboration will help accelerate research and treatments for CMT patients worldwide….
Nanoparticles for CMT1A, CMT1B, and CMTX1: A New Frontier in Gene Therapy
…Research Today Not yet registered with Patients as Partners in Research? Click the button below to register today! Registering ensures you are the first in line for any CMT research…
Development of Advanced Research Diagnostic Capabilities for the CMT Community
…to address this issue by aggregating genetic data (panels, exomes, and genomes) from patients into a common database. This database is available to qualified researchers in the field and this…
Advancing the Understanding of CMT2A and CMT2F: A Call to Beat CMT
The Charcot-Marie-Tooth Association (CMTA), through its Strategy To Accelerate Research (STAR) initiative, is proud to support groundbreaking research that seeks to deepen our understanding of CMT2A and CMT2F, two axonal…