2017_Fall_CMTA_Report
…may use to aid and supplement a doctor’s treatment. CMTA LEADERSHIP CMTA STAFF Amy J. Gray, CEO BOARD OF DIRECTORS Gilles Bouchard, Chairman Gary Gasper, Treasurer Herb Beron, Secretary Thomas…
2017_Fall_CMTA_Report
…may use to aid and supplement a doctor’s treatment. CMTA LEADERSHIP CMTA STAFF Amy J. Gray, CEO BOARD OF DIRECTORS Gilles Bouchard, Chairman Gary Gasper, Treasurer Herb Beron, Secretary Thomas…
CMTAreportSummer2023spreads
…treatments at a Zoom Patient Listening Session April 18. They also expressed the need for treatments that will slow the progression of muscle wasting. FDA Patient Listening Sessions provide a…
2022.09.12_PREMIER-OLE_FPI_EN
…2022 has shown a good safety profile and continuous treatment effect of PXT3003 measured on the ONLS after 5 years of total treatment time. 123 Patients with mild-to-moderate CMT1A are…
CMTAreportSummer2022web
…quite strong compared to the beginning of treatment. I always used a handrail going up and down stairs before treatment, but now I walk up and down with some pace…
CMTAreportSpring2023spreads
…CMTA Partner On ASO Treatment for CMT1A 2023 ‘Pivotal’ Year for PXT3003 Treatment For CMT1A as Manufacturing Shifts to U.S. CMTA partner Pharnext announced Jan. 26 that it has completed…
CMTAfall2022web
…virtual meeting June 7. Mackenzie shared valuable information on treatment goals for bracing, treatment options, who’s a candi- date, what to expect at a visit and much more. The branch…
CMTAfall2022web
…virtual meeting June 7. Mackenzie shared valuable information on treatment goals for bracing, treatment options, who’s a candi- date, what to expect at a visit and much more. The branch…
CMTAreportSummer2022web
…quite strong compared to the beginning of treatment. I always used a handrail going up and down stairs before treatment, but now I walk up and down with some pace…
Repurposing Drugs for CMT1A: An Encouraging Approach
…nerve cells will alleviate CMT symptoms and slow disease progression. This innovative approach to CMT1A treatment involves repurposing an existing FDA-approved drug, which could expedite the availability of a new…