2019_Spring_CMTA_Report
…mice led to increased protein levels and tested whether treatment at later stages of the disease led to improvement like that seen for treatment in the early stages. The target…
2019_Spring_CMTA_Report
…mice led to increased protein levels and tested whether treatment at later stages of the disease led to improvement like that seen for treatment in the early stages. The target…
CMT Respiratory Impairment Final
…Common treatment approaches for restrictive and obstructive lung disease are basically oxygen as needed, an inhaler or two, and nebulizer treatments. Oxygen is used to treat hypoxemia/hypoxia, and inhalers/nebulizer treatments…
CMTAreportSummer2023spreads
…treatments at a Zoom Patient Listening Session April 18. They also expressed the need for treatments that will slow the progression of muscle wasting. FDA Patient Listening Sessions provide a…
CMTAreportSummer2022web
…quite strong compared to the beginning of treatment. I always used a handrail going up and down stairs before treatment, but now I walk up and down with some pace…
2022.09.12_PREMIER-OLE_FPI_EN
…2022 has shown a good safety profile and continuous treatment effect of PXT3003 measured on the ONLS after 5 years of total treatment time. 123 Patients with mild-to-moderate CMT1A are…
CMTAreportSummer2022web
…quite strong compared to the beginning of treatment. I always used a handrail going up and down stairs before treatment, but now I walk up and down with some pace…
CMTAreportSpring2023spreads
…CMTA Partner On ASO Treatment for CMT1A 2023 ‘Pivotal’ Year for PXT3003 Treatment For CMT1A as Manufacturing Shifts to U.S. CMTA partner Pharnext announced Jan. 26 that it has completed…
CMTAfall2022web
…virtual meeting June 7. Mackenzie shared valuable information on treatment goals for bracing, treatment options, who’s a candi- date, what to expect at a visit and much more. The branch…
CMTAfall2022web
…virtual meeting June 7. Mackenzie shared valuable information on treatment goals for bracing, treatment options, who’s a candi- date, what to expect at a visit and much more. The branch…