The Summer 2023 CMTA Report

…of interest: CMT Patients Urge Faster Clinical Trials Applied Therapeutics Research Update DTx Treatment for CMT1A Under the Microscope: ASOs CMTA Funds Preclinical Work on CMT1B Mice Summer with CMT…

The Summer 2021 CMTA Report

…Gray Celebrating Steve (and his 2 decades of fundraising) CMTA Awards Züchner $300,000 for Gene Discovery Work CMTA Awards $100,000 to Explore Potential 1X Treatment CMTA-STAR Awards $1.1 Million in…

All Other Types

…CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be of therapeutic benefit across a variety of CMT types. PROJECT GOAL:…

Find Research by My CMT Type/Subtype

…so essentially the abnormal protein is blocking the function of the working protein and somehow treatment will need to silence that abnormal copy or cut it out. If it can…

CMT2S Research

…using mouse models of several forms of CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be of therapeutic benefit across…

CMT2D Research

…Scientific Advisory Board, is using mouse models of several forms of CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be…

CMT1X Research

…help advance development of treatments for other types of CMT affecting Schwann cells, as a similar AAV approach can be applied to CMT1A and other subtypes of CMT1. PROJECT GOAL:…

CMTA-STAR Research for Axonal Forms of CMT

…to the market in the near future. The CMTA’s funding and operations focus is on translational research that will lead as directly as possible to therapeutic treatments for CMT. Axonal…

Who Inspires You to Give?

…that seeing the CMTA’s research progress and knowing that she is leaving a legacy and contributing to a treatment/cure inspires her to give. Under the CMTA’s Strategy to Accelerate Research,…