Gene Therapy for CMT1A, 1B, and X1: Progress in Nanoparticles
…to reach where they are needed: Schwann cells. This testing will help the team figure out the best way to deliver the treatment in the future. The next phase involves…
Breakthrough in CMT1A Research: Community Efforts Drive Success of Dental Stem Cell Model
…for future drug screening and treatment development beyond CMT1A, including CMT1E, HNPP, CMTX1 (aka CMT1X, CMTX), CMT2A, CMT2C, CMT2T, and CMT4A—the additional subtypes from which donations were received. Register With…
CMTA Partners with Actio Bio on CMT2C Focus Group
…future treatment goals. Moderated by CMTA, patient participants were given a platform to directly share their experiences in a manner that will contribute towards new advancements in research and the…
Recap: 2024 CMTA Patient & Research Summit
…in potential CMT treatments and ongoing projects aimed at finding a cure. Help for Today Attendees of the 2024 CMTA Patient & Research Summit The Summit provided attendees with many…
Exploring New Therapeutic Pathways for CMT1B: UPR Activation
…developing a potential treatment for CMT1B. This groundbreaking work, led by Maurizio D’Antonio, PhD, focuses on activating the Unfolded Protein Response (UPR), targeting the fundamental issue caused by mutations in…
Central Tennessee CMTA Branch Meeting (Virtual)
08/26/2024 @ 6:00 pm – 7:00 pm – Please join us (via Zoom) for the next meeting of the Central Tennessee CMTA Branch on Monday, August 26th at 6 pm Central Time when we will gather virtually to discuss what to do after receiving a diagnosis of CMT. The session will cover the essential information on available resources, treatment options, and practical strategies […]
Repurposing Drugs for CMT1A: An Encouraging Approach
…nerve cells will alleviate CMT symptoms and slow disease progression. This innovative approach to CMT1A treatment involves repurposing an existing FDA-approved drug, which could expedite the availability of a new…
CMTA Announces New Center of Excellence at Duke University Hospital
The Charcot-Marie-Tooth Association (CMTA), the world’s largest philanthropic funder of research aimed at bringing treatments to patients and improving the lives of those living with Charcot-Marie-Tooth disease (CMT), is thrilled…
Summer 2024 CMTA Report: A Season of Renewal and Progress
…intelligence revolutionizes CMT diagnosis, treatment, and management with a dedicated feature by CMTA Chief Research Officer Katherine Forsey, PhD, on page 20 in her column, Under the Microscope. Additionally, community…
CMT-SORD: Share Your Story
…help accelerate advancements towards treatments and, ultimately, a cure for this disease. The main goal of this CMT research project is to understand better how CMT-SORD affects the person in…