CMT2D Research

…Scientific Advisory Board, is using mouse models of several forms of CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be…

CMT1X Research

…help advance development of treatments for other types of CMT affecting Schwann cells, as a similar AAV approach can be applied to CMT1A and other subtypes of CMT1. PROJECT GOAL:…

Help CMTA Develop Clinical Trials in a Dish

…that are affected by CMT disease. If we can study these cells, we can increase our understanding of CMT and test the effectiveness of new treatments more quickly. Stem cells…

Who Inspires You to Give?

…that seeing the CMTA’s research progress and knowing that she is leaving a legacy and contributing to a treatment/cure inspires her to give. Under the CMTA’s Strategy to Accelerate Research,…

CMTA Lunch & Learn: CMT 1A-focused Patients as Partners in Research Town Hall

09/20/2023 @ 12:00 pm – 1:00 pm – Please join us on September 20th at 12:00 p.m. Eastern Time for our next Lunch & Learn education meeting when we will welcome guest speakers John Svaren and Gilles Bouchard. Dr. Svaren and Gilles will be sharing a CMT 1A STAR research update to include the following: the latest information about DTx-1252, the potential life-changing […]

Inside Innovation | Education Event & Lab Tour

04/09/2025 @ 12:30 pm – 4:30 pm – Join us for a special event with CMTA-STAR Alliance Partner, Actio Biosciences on Wednesday, April 9 from 12:30 p.m. – 4:30 p.m. Pacific Time. CMT community members are invited to spend the afternoon learning about the world-class research Actio Biosciences is doing in CMT 2C/TRPV4+, and attendees will also get to tour Actio Biosciences research […]

Clinical Summit 2023 – Impact Report

…increasing levels of disability. CMT affects around 1 in every 2500 people, there are over 100 known causative gene mutations and there is currently no curative treatment available to the…

CMTA Partners with Actio Bio on CMT2C Focus Group

…future treatment goals. Moderated by CMTA, patient participants were given a platform to directly share their experiences in a manner that will contribute towards new advancements in research and the…