Page 29 - 2021 Spring CMTA Report - Special Research Edition
P. 29

A X O N A L  T Y P E S



 STAR ALLIANCE PARTNERS  THERAPY TYPE  DRUG  DEVELOPMENT STAGE
 Discovery   Research Tools   Preclinical   Phase1   Phase2   Phase3
 Passage Bio + University of Pennsylvania   Gene Therapy         Preclinical
 Regenacy Pharmaceuticals*   Small Molecule         Preclinical
 STAR Biotech Partner E   Small Molecule         Preclinical
 STAR Biotech Partner A   Small Molecule         Preclinical
 STAR Biotech Partner F   Peptide         Preclinical
 2A  Universities of Iowa & Wisconsin   Biomarkers         Preclinical
 University of Iowa   Respiratory Study                P2
 University of Pennsylvania   Animal Models      Laboratory
 STAR Partner G   Small Molecule   Discovery
 Gladstone Institute (UCSF)   Gene Therapy (CRISPR)   Discovery
 Washington University   Small Molecule   Research Interest


 STAR ALLIANCE PARTNERS  THERAPY TYPE  DRUG  DEVELOPMENT STAGE
 Discovery   Research Tools   Preclinical   Phase1   Phase2   Phase3

 2D  Jackson Laboratory   SARM1/Target Validation             Preclinical
 Jackson Laboratory
    Preclinical
 HDAC6/Target Validation
 STAR ALLIANCE PARTNERS  THERAPY TYPE  DRUG  DEVELOPMENT STAGE
 Discovery   Research Tools   Preclinical   Phase1   Phase2   Phase3
 Regenacy Pharmaceuticals*   Small Molecule         Preclinical
 STAR Biotech Partner D   Biological         Preclinical
 Nationwide Children’s Hospital + Ohio State University   Gene Therapy         Preclinical
 Columbia University   Small Molecule         Preclinical
 2E  University of Miami   Small Molecule         Preclinical
 Gladstone Institute (UCSF)   Gene Therapy (CRISPR)         Preclinical
 Jackson Laboratory   SARM1/Target Validation         Preclinical
 Jackson Laboratory   HDAC6/Target Validation         Preclinical
 Columbia University   Animal Model      Laboratory

 DRUG  DEVELOPMENT STAGE
 STAR ALLIANCE PARTNERS  THERAPY TYPE
 Discovery   Research Tools   Preclinical   Phase1   Phase2   Phase3
 Jackson Laboratory   SARM1/Target Validation         Preclinical
 2S  Jackson Laboratory   HDAC6/Target Validation         Preclinical


 STAR ALLIANCE PARTNERS  THERAPY TYPE  DRUG  DEVELOPMENT STAGE
 Discovery   Research Tools   Preclinical   Phase1   Phase2   Phase3
 ALL TYPES Psychogenics + Cleveland Clinic + Charles River   Research & Clinical Tools  Laboratory  Preclinical
    Preclinical
 Preclinical Testing Partners
 Inherited Neuropathy Consortium
 Stem Cell Lines
 New York Stem Cell Foundation
 University of Miami
 Jackson Laboratory   Gene Identification   Discovery  Laboratory
 Animal Models




                                                                      Kenneth is a martial arts
                                                                      instructor for children and adults with
                                                                      special needs. He has CMT1X.




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